Tackling a Novel Therapeutic and its Commercial Potential for the Tumor Lysis Syndrome
Student: Emily Russo, 2017-2018
In the United States, an orphan disease is defined as a rare disorder affecting less than 200,000 people. A majority of orphan disease patients lack the proper treatment they need. This thesis project will focus on the treatment of these diseases and assess the commercial potential of a novel therapeutic for the tumor lysis syndrome (TLS). This rare condition is characterized by a combination of one or more medical conditions resulting from adverse effects of chemotherapy treatment of blood cancers. Through customer validation from key opinion leaders such as nephrologists, oncologists, and hematologists, as well as from current and former patients, important insights will be analyzed to determine the next viable step. The ultimate goal is to address the unmet medical needs of TLS patients and significantly improve their quality of life.